Decoding Neurological Disease. Building Medicines.

CELLTIUM is developing precision therapies for CMT1A and related neurological disorders. By uniting deep biological insights with our proprietary PRECISION™ platform, we are accelerating the path from discovery to life-changing treatments.

A New Model for Neurotherapeutics
At the core of our approach, we integrate quantitative phenotyping, multimodal data, and AI into a unified discovery engine. This framework streamlines target identification, lead optimization, and strategic decision-making.

Targeting the Core Biology
We are advancing a robust portfolio of mechanistically distinct small molecules. Rather than simply managing symptoms, our therapies are designed to address the root causes of peripheral neuropathies and actively restore nerve function.

Partner With Us

We welcome strategic collaborations with investors and pharmaceutical leaders to propel our lead CMT1A programs into the clinic and expand our platform’s reach across new indications.

Interested in Our CMT1A Program?

MEET US AT

June 22–25, 2026 | San Diego, CA

April 28–30, 2026 | Seoul, KR

A New Model for Neurotherapeutics At the core of our approach, we integrate quantitative phenotyping, multimodal data, and AI into a unified discovery engine. This framework streamlines target identification, lead optimization, and strategic decision-making.

Targeting the Core Biology We are advancing a robust portfolio of mechanistically distinct small molecules. Rather than simply managing symptoms, our therapies are designed to address the root causes of peripheral neuropathies and actively restore nerve function.

Interested in Our CMT1A Program?

A New Model for Neurotherapeutics
At the core of our approach, we integrate quantitative phenotyping, multimodal data, and AI into a unified discovery engine. This framework streamlines target identification, lead optimization, and strategic decision-making.

Targeting the Core Biology
We are advancing a robust portfolio of mechanistically distinct small molecules. Rather than simply managing symptoms, our therapies are designed to address the root causes of peripheral neuropathies and actively restore nerve function.